2011/02/10
Designed endonucleases in gene therapy for the Bubble Boy syndrome
A collaborative work from research groups at CIC bioGUNE, CNIO, CRG and Cellectis shows how meganucleases can be tailored to induce homologous recombination in human cells and repair the defective gene causing severe combined immunodeficiency (SCID).
See a large version of the first picture